A Study of LOXO-435 in Participants With Cancer With a Change in a Gene Called FGFR3

ID#: NCT05614739

Age: 18 years - 66+

Gender: All

Healthy Subjects: No

Study Phase: Phase 1

Recruitment Status: Recruiting

Start Date: January 19, 2023

End Date: June 01, 2025

Contact Information:
There may be multiple sites in this clinical trial. 1-877-CTLILLY (1-877-285-4559) or
13176154559
Summary: The main purpose of this study is to learn more about the safety, side effects, and effectiveness of LOXO-435. LOXO-435 may be used to treat cancer of the cells that line the urinary system and other solid tumor cancers that have a change in a particular gene (known as the FGFR3 gene). Participation could last up to 30 months (2.5 years) and possibly longer if the disease does not get worse.
Eligibility:

Inclusion Criteria:

- Have solid tumor cancer with an FGFR3 pathway alteration on molecular testing in tumor or blood sample that is deemed as actionable.

- Cohort A1 (Dose Escalation): Presence of an alteration in FGFR3 or its ligands.

- Cohort A2 (Dose Optimization): Histological diagnosis of urothelial cancer (UC) that is locally advanced or metastatic with a qualifying FGFR3 alteration.

- Cohorts B1, B2 and B3 (Dose Expansion): Histological diagnosis of urothelial cancer that is locally advanced or metastatic with a prespecified activating FGFR3 alteration.

- Cohort C (Dose Expansion): Must have histological diagnosis of a non-urothelial solid tumor malignancy that is locally advanced or metastatic with a prespecified activating FGFR3 alteration.

- Measurability of disease:

- Cohort A1: Measurable or non-measurable disease as defined by Response Evaluation Criteria in Solid Tumors v 1.1 (RECIST v1.1)

- Cohorts A2, B1, B2, B3, and C1: Measurable disease required as defined by RECIST v1.1

- Have adequate archival tumor tissue sample available or undergo a screening biopsy if allowed per country-specific regulations.

- Have an Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.

- Prior Systemic Therapy Criteria:

- Cohort A1/C1: Participant has received all standard therapies for which the participant was deemed to be an appropriate candidate by the treating Investigator; OR the participant is refusing the remaining most appropriate standard of care treatment; OR there is no standard therapy available for the disease. There is no restriction on number of prior therapies.

- Cohort A2/B1/B2/B3: Participants must have received at least one prior regimen in the advanced or metastatic setting. There is no restriction on number of prior therapies.

- FGFR inhibitor specific requirements:

- Cohort A1/A2: Prior FGFR inhibitor treatment is permitted, but not required.

- Cohort B1: Participants must have been previously treated with a FGFR inhibitor.

- Cohort B2, B3, C1: Participants must be FGFR inhibitor naïve.

Exclusion Criteria:

- Participants with primary central nervous system (CNS) malignancy.

- Known or suspected history of uncontrolled CNS metastases.

- Current evidence of corneal keratopathy or retinal disorder.

- Have a history and/or current evidence of extensive tissue calcification.

- Any serious unresolved toxicities from prior therapy.

- Significant cardiovascular disease.

- Prolongation of the QT interval corrected for heart rate using Fridericia's formula (QTcF).

- Active uncontrolled systemic infection or other clinically significant medical conditions.

- Participants who are pregnant, lactating, or plan to breastfeed during the study or within 6 months of the last dose of study treatment. Participants who have stopped breastfeeding may be enrolled.